DMD treatment SMT-01, a cell replacement therapy, received FDA orphan drug and rare pediatric disease designations.

For a long time, columnist Robin Stemple resisted using a walker to navigate around his home, but eventually, he had to put ...

Last Saturday, I had the honor of participating in the third Singapore Health Patient Advocate Connection event (SPACe) ...

Kevin Schaefer, the associate director of community content at Bionews, the parent company of this website, recently shared a thought-provoking article from Psychology Today titled “How Chronic ...

Losmapimod, an investigational medication from Fulcrum Therapeutics, failed to significantly outperform a placebo at ...

In my recent columns, I’ve shared several challenges we’ve faced in the past months of my family’s journey with Duchenne muscular dystrophy (DMD). My accessible van will be in the shop for the ...

My life has recently been a whirlwind of activity. Now that the dust is finally settling, I’ve taken advantage of the relative quiet to take inventory of my family. An inventory of my family? What ...

Esteban holds a Master of Science in Immunology from the Instituto Politécnico Nacional in Mexico, focused on inflammation and metabolism. With five years of experience as a Medical Science Liaison, ...

The U.S. Food and Drug Administration granted rare pediatric disease designation to NS-050/NCNP-03, an exon-skipping DMD ...