StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.
Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is a big problem: size.
It's hoped a first-of-its-kind computer model of nasal cavity will help develop treatments for diseases like Parkinsons and Alzheimers.